INV04 16:45-17:15
Gloria Gonzalez-Aseguinolaza, CIMA, Pamplona ⓘ
Gene therapy for liver inherited diseases
INV05 17:15-17:45
Martina Marinello, Genethon, Evry ⓘ
Gene therapy of spinal muscular atrophy by single-stranded AAV9 vectors
INV06 17:45-18:15
Frederic Thalheimer, Paul-Ehrlich-Institut, Langen ⓘ
Receptor targeted viral vectors for In vivo delivery
OR03 18:15-18:30
Celia Sourd, Genethon, UMR_S951, Inserm, Univ Evry, Université Paris Saclay, EPHE
An AAVpo1A1 vector expressing MTM1 corrects skeletal muscle pathology with detargeted liver transduction in myotubular myopathy mice
OR04 18:30-18:45
Mathieu Mével, Nantes Université, TaRGeT - Translational Research in Gene Therapy, INSERM UMR 1089, CHU de Nantes
Chemically tyrosine modified AAV vectors: an innovative technological platform to boost gene delivery